Nanoscope's gene therapy offers hope for patients blinded by inherited retinal disease
FierceBiotech - 26-Mar-2024Phase 2 trial results show significant vision improvement, plans for FDA approval
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Biopharmaceutical company developing gene therapies to cure retinal diseases
Nanoscope Therapeutics is a clinical-stage biopharmaceutical company developing gene therapies to cure genetic diseases that cause vision impairment and blindness. These diseases include Retinitis Pigmentosa, Dry Age-related Macular Degeneration (AMD), and Stargardt Disease. The company is developing a proprietary platform technology, using light-sensitive molecules, called Multi-Characteristic Opsins (MCO), and light-assisted gene delivery for giving sight to the millions of blind individuals.
The company's lead product, MCO-010, has been granted Orphan Drug and Fast Track designation by the US FDA for both retinitis pigmentosa (RP) and Stargardt disease.
Visit website: https://nanostherapeutics.com/
Details last updated 08-Apr-2024
Phase 2 trial results show significant vision improvement, plans for FDA approval